Kupatt, C.* ; Windisch, A.* ; Moretti, A.* ; Wolf, E.* ; Wurst, W. ; Walter, M.C.*
Genome editing for Duchenne muscular dystrophy: A glimpse of the future?
Gene Ther. 28, 542–548 (2021)
Rollier, C.S.* ; Verschoor, E.J.* ; Verstrepen, B.E.* ; Drexhage, J.A.R.* ; Paranhos-Baccala, G.* ; Liljeström, P.* ; Sutter, G. ; Arribillaga, L.* ; Lasarte, J.J.* ; Bartosch, B.* ; Cosset, F.L.* ; Inchauspe, G.* ; Heeney, J.L.*
T- and B-cell responses to multivalent prime-boost DNA and viral vectored vaccine combinations against hepatitis C virus in non-human primates.
Gene Ther. 23, 753-759 (2016)
Pfeifer, C.* ; Aneja, M.K. ; Hasenpusch, G.* ; Rudolph, C.*
Adeno-associated virus serotype 9-mediated pulmonary transgene expression: effect of mouse strain, animal gender and lung inflammation.
Gene Ther. 18, 1034-1042 (2011)
Pike, L.S.* ; Tannous, B.A.* ; Deliolanis, N.C. ; Hsich, G.* ; Morse, D.* ; Tung, C.H.* ; Sena-Esteves, M.* ; Breakefield, X.O.*
Imaging gene delivery in a mouse model of congenital neuronal ceroid lipofuscinosis.
Gene Ther. 18, 1173-1178 (2011)
Westermann, J.* ; Flörcken, A.* ; Willimsky, G.* ; van, Lessen, A.* ; Kopp, J.* ; Takvorian, A.* ; Jöhrens, K.* ; Lukowsky, A.* ; Schönemann, C.* ; Sawitzki, B.* ; Pohla, H. ; Frank, R. ; Dörken, B.* ; Schendel, D.J. ; Blankenstein, T.* ; Pezzutto, A.*
Allogeneic gene-modified tumor cells (RCC-26/IL-7/CD80) as a vaccine in patients with metastatic renal cell cancer: A clinical phase-I study.
Gene Ther. 18, 354-363 (2011)
Kutscher, S. ; Allgayer, S. ; Dembek, C.J. ; Bogner, J.R.* ; Protzer, U. ; Goebel, F.D.* ; Erfle, V.* ; Cosma, A.
MVA-nef induces HIV-1-specific polyfunctional and proliferative T-cell responses revealed by the combination of short- and long-term immune assays.
Gene Ther. 17, 1372-1383 (2010)
Riddell, S.R.* ; Protzer, U.
Grafting chimeric antigen receptors to redirect T cells: Carving the CAR.
Gene Ther. 17, 1191-1192 (2010)
Bauer, M. ; Kinkl, N. ; Meixner, A. ; Kremmer, E. ; Riemenschneider, M.* ; Förstl, H.* ; Gasser, T.* ; Ueffing, M.
Prevention of interferon-stimulated gene expression using microRNA-designed hairpins.
Gene Ther. 16, 142-147 (2009)
Rothenaigner, I. ; Kramer, S. ; Meggendorfer, M. ; Rethwilm, A.* ; Brack-Werner, R.
Transduction of human neural progenitor cells with foamy virus vectors for differentiation-dependent gene expression.
Gene Ther. 16, 349-358 (2009)
Hellebrand, E. ; Mautner, J. ; Reisbach, G. ; Nimmerjahn, F. ; Hallek, M.* ; Mocikat, R. ; Hammerschmidt, W.
Epstein-Barr virus vector-mediated gene transfer into human B cells: Potential for antitumor vaccination.
Gene Ther. 13, 150-162 (2006)
Hettich, E. ; Janz, A. ; Zeidler, R.* ; Pich, D. ; Hellebrand, E. ; Weissflog, B. ; Moosmann, A. ; Hammerschmidt, W.
Genetic design of an optimized packaging cell line for gene vectors transducing human B cells.
Gene Ther. 13, 844-856 (2006)
Dumortier, J.* ; Schönig, K.* ; Oberwinkler, H.* ; Löw, R.* ; Giese, T.* ; Bujard, H.* ; Schirmacher, P.* ; Protzer, U.*
Liver-specific expression of interferon gamma following adenoviral gene transfer controls hepatitis B virus replication in mice.
Gene Ther. 12, 668-677 (2005)
Kofler, D.M. ; Buning, H.* ; Mayr, C. ; Bund, D. ; Baumert, J.J. ; Hallek, M. ; Wendtner, C.-M.
Engagement of the B-cell antigen receptor (BCR) allows efficient transduction of ZAP-70-positive primary B-CLL cells by recombinant adeno-associated virus (rAAV) vectors.
Gene Ther. 11, 1416-1424 (2004)
Buning, H.* ; Ried, M.U.* ; Perabo, L.* ; Gerner, F.M* ; Huttner, N.A.* ; Enssle, J.* ; Hallek, M.
Receptor targeting of adeno-associated virus vectors.
Gene Ther. 10, 1142-1151 (2003)
Schendel, D.J. ; Falk, C.S. ; Nößner, E. ; Maget, B. ; Kressenstein, S. ; Urlinger, S.* ; Tampé, R.* ; Gansbacher, B.*
Gene transfer of human interferon gamma complementary DNA into a renal cell carcinoma line enhances MHC-restricted cytotoxic T lymphocyte recognition but suppresses non-MHC-restricted effector cell activity.
Gene Ther. 7, 2-10 (2000)
Selmayr, M. ; Strehl, J. ; Kremer, J.-P. ; Kremmer, E. ; Doenecke, A.* ; Hallek, M.* ; Menzel, H.* ; Thielemans, K.* ; Thierfelder, S. ; Mocikat, R.
Induction of tumor immunity by autologous B lymphoma cells expressing a genetically engineered idiotype.
Gene Ther. 6, 778-784 (1999)